When a disease is rare, listening shouldn’t be. That is why we believe working collaboratively and with transparency unlocks our potential to do more.

Looking out for You

That’s why we partner with a range of international and regional rare disease advocacy groups to learn and co-develop programs to empower patients and caregivers. Find resources, advocates, and allies to help you on your journey.

We encourage patient organizations to visit our sponsorship portal for more information. Our goal is to provide compliant support to organizations and connect them with resources for the benefit of the rare disease community.

Sponsorship Portal

As the science evolves, our focus is on finding therapies for the following key rare disease areas:

Inborn Errors of Metabolism


Fabry Disease

Nephropathic Cystinosis

Rare Hematology


Sickle Cell Disease

Rare Immunodeficiencies

Adenosine Deaminase Severe Combined Immunodeficiency (ADA-SCID)

Lean on us with the Chiesi Total Care Program

Patients with rare diseases can find the support they need with the Chiesi Total Care Program.

Let's Go

Expanded Access Programs

Expanded Access, sometimes referred to as compassionate use, may be an option for certain individuals with serious or life-threatening conditions or diseases who have no satisfactory or comparable alternative therapy to treat the disease or condition involved. Patients who qualify for a clinical trial on the Investigational Product requested are not eligible for Expanded Access.

For a full listing of Chiesi clinical trials, please visit www.clinicaltrials.gov.

For more information on criteria for access or submitting requests, please click here: https://www.chiesiusa.com/contact-us/expanded-access-programs

To submit a request for Expanded Access, the treating physician must submit the request through this link: https://chiesi.versaic.com

*Chiesi Global Rare Diseases reserves the right to revise this Policy at any time. Expanded Access is not available in areas where forbidden by law or regulation including ruling by country or region specific regulatory bodies, importation requirements, and/or Ethics Committee or Institutional Review Board.

Learn More about Chiesi Global Rare Diseases

Find Treatments


Discover treatments that are helping to change the rare disease landscape.

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Find Treatments


Discover innovative treatments that are helping to change the rare disease landscape.

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See Pipeline


Explore rare disease therapies under development.

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See Pipeline


Explore novel therapies under development

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About Us


Learn more about who we are and why we care about improving the lives of people with rare diseases.

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Join the Family

the Family

Interested in a career at Chiesi Global Rare Diseases? We’d love to hear from you.

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